Michela Pantaleoni

Company: Napo Therapeutics

Job title: Chief Market Access Officer

Seminars:

Fireside Discussion: Expanding Compassionate Use for Rare & Small Patient Populations: Emerging Models & Ethical Imperative 9:30 am

• Adapting compassionate use frameworks for ultra-rare conditions as regulatory and ethical models evolve to support access without robust trial data • Enabling cross-stakeholder coordination through pilot initiatives like the UK’s Rare Therapies Launchpad to build infrastructure for small population access • Balancing safety, speed, and evidence generation for regulators, clinicians, and sponsors supporting compassionate…Read more

day: Day 2