Real-World Data in EU Early Access Programmes: GSK Case Study

  • Defining the minimal dataset that aligns with both regulatory and payor requirements while maintaining feasibility in early access settings
  • Addressing variability in RWD collection across EU countries and navigating differing expectations from regulators and health technology assessment (HTA) bodies
  • Overcoming data collection limitations in different EAP models, from named-patient programs to broader early access frameworks