Ensuring People with Rare Diseases Receive Early Access to Treatments: A Case Study with Lumevoq Gene Therapy in Leber Hereditary Optic Neuropathy

Time: 2:30 pm
day: Day One

Details:

  • Running a Gene Therapy Early Access Programme for a rare disease
  • Outlining requirements and global strategies required
  • Understanding the timings and urgency for acute diseases

Speakers: